PROTEOMICS
Proteomics is the large scale study of proteins within an organism. For HD, this is a technique we use to define new
interactions with the huntingtin protein that are relevant to understand how huntingtin works, how huntingtin is toxic when
polyglutamine expanded, and define new targets for drug targeting for HD.
The basis for this work is protein affinity chromatography, a technique in which we use fragments of huntingtin as ligand for
purification of proteins from a cellular extract. This is a commonly used technique to define interactors with proteins,
however we have adapted this technique to help define true interactors from the very high noise that is inherent to this
method, by the use of:
1. varying ligand protein concentrations
2. fractionated extracts
3. control ligands with subtle mutations defined in vivo.
4. different elution conditions
Re-iterative Protein Micro Affinity Chromatography and Validation of Direct Interacting Proteins. A. Pure Htt Exon1
Q16 or Q46 is covalently linked to active ester agarose matrix and packed into a 20ul microcolumn for chromatography with
500ml of mouse whole cell brain extracts or membrane detergent extracts under physiological salt concentration. After
loading and washing, proteins and complexes are eluted under high salt conditions to remove proteins from the affinity
column and disrupt higher order complexes. Fractions are dialysed back to physiological salt concentrations and re-
chromatographed over a new column. After a second load and wash, Final elution is salt step gradient, followed by high salt
and 0.1% SDS across columns of varying ligand concentrations. Liquid eluates are then analysed by mass spectrometry to
identify proteins (LC-MS-MS). B. Identified proteins will be expressed and purified from E.coli and passed over ligand
columns, or placed into reciprocal co-immunoprecipitation experiments to determine direct interactions with no other factors
present, at this point, affinity constants can be measured. C. Protein cDNAs will
be fused to AFP variants and expressed in culture cells, either primary neuronal
or other, for fluorescent microscopy-based assays. D. Interactions will be further
defined using site-directed mutagenesis of the polyglutamine disease protein,
effects of cell biological assay drugs like leptomycin B and cell biology stains for
ER, DNA, RNA, lysosome, endosome, mitochondria, as well as long time course
measurements of dynamics and short measurements by FRAP and FRET. (click
on diagram to enlarge)